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We would love to hear from you

Whether you are an individual or a family facing the challenges of a rare disease with an unmet need, a healthcare professional caring for rare disease patients or you are interested in getting involved with our development, please reach out to us. We would love to hear from you.


Austin Headquarters

4200 Marathon Blvd., Suite 200
Austin, Texas 78756
(512) 215-2630

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Ames Office

2503 South Loop Drive
Ames, IA 50010
(515) 296-5555

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